World Clinical Drugs, Volume. 46, Issue 7, 715(2025)
A new drug for the treatment of hereditary transthyretin amyloid polyneuropathy: eplontersen
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[22] [22] ClinicalTrials. A study to assess the long-term safety and efficacy of eplontersen (formerly known as ION-682884, IONIS-TTR-LRx and AKCEA-TTR-LRx) in patients with hereditary transthyretin-mediated amyloid polyneuropathy [EB/OL]. (2023-10-06) [2024-12-16]. https://www.clinicaltrials.gov/study/NCT05071300.
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[24] [24] ClinicalTrials. EPIC-ATTR: a study to evaluate the effect of eplontersen on the transthyretin reduction and long-term safety in Chinese subjects with transthyretin amyloid cardiomyopathy (EPIC-ATTR) [EB/OL]. (2024-01-08) [2024-12-16]. https://www.clinicaltrials.gov/study/NCT06194825.
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ZHU Haibin, WANG Yue, LIAO Xiaolan, WU Tingting, YU Zicheng. A new drug for the treatment of hereditary transthyretin amyloid polyneuropathy: eplontersen[J]. World Clinical Drugs, 2025, 46(7): 715
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Received: Dec. 28, 2024
Accepted: Aug. 26, 2025
Published Online: Aug. 26, 2025
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